{"id":8394,"date":"2021-12-15T16:54:43","date_gmt":"2021-12-15T16:54:43","guid":{"rendered":"https:\/\/epitomestaging.com\/tnc\/?page_id=8394"},"modified":"2025-01-31T17:43:18","modified_gmt":"2025-01-31T17:43:18","slug":"accomplishments","status":"publish","type":"page","link":"https:\/\/epitomestaging.com\/tnc\/accomplishments\/","title":{"rendered":"Accomplishments"},"content":{"rendered":"

[et_pb_section fb_built=”1″ admin_label=”Home 2 Content Pg” _builder_version=”4.16″ _module_preset=”default” background_color=”#bbe4ed” background_image=”https:\/\/epitomestaging.com\/tnc\/wp-content\/uploads\/2022\/02\/rsz-tnc-header-about-1000×200-1.jpg” background_size=”initial” background_position=”top_center” width_phone=”auto” width_last_edited=”off|desktop” max_width_last_edited=”off|desktop” module_alignment=”center” min_height_tablet=”300px” min_height_last_edited=”off|desktop” height=”200px” height_tablet=”154px” height_phone=”100px” height_last_edited=”on|phone” max_height_tablet=”300px” max_height_phone=”300px” max_height_last_edited=”off|desktop” custom_margin=”0px||0px||false|false” custom_padding=”0px||0px||false|false” top_divider_height_tablet=”” top_divider_height_phone=”50px” top_divider_height_last_edited=”on|phone” bottom_divider_style=”curve” bottom_divider_color=”#FFFFFF” bottom_divider_height=”70px” bottom_divider_arrangement=”above_content” bottom_divider_height_tablet=”70px” bottom_divider_height_phone=”50px” bottom_divider_height_last_edited=”on|desktop” background_last_edited=”on|phone” background_image_phone=”https:\/\/epitomestaging.com\/tnc\/wp-content\/uploads\/2022\/02\/rsz-tnc-mobile-stars.jpg” background_enable_image_phone=”on” parallax_tablet=”off” parallax_phone=”off” background_size_tablet=”contain” background_size_phone=”initial” background_position_tablet=”top_center” background_position_phone=”top_right” module_alignment_tablet=”right” module_alignment_phone=”left” module_alignment_last_edited=”off|desktop” locked=”off” global_colors_info=”{}”][et_pb_row column_structure=”1_2,1_2″ use_custom_gutter=”on” gutter_width=”1″ _builder_version=”4.16″ _module_preset=”default” module_alignment=”center” custom_margin=”0px||||false|false” custom_padding=”0px||||false|false” global_colors_info=”{}”][et_pb_column type=”1_2″ _builder_version=”4.16″ _module_preset=”default” global_colors_info=”{}”][et_pb_text _builder_version=”4.16″ _module_preset=”default” z_index=”10″ custom_margin=”30px||||false|false” global_colors_info=”{}”]<\/p>\n

About Us<\/h1>\n

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Accomplishments<\/h2>\n

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RSZ TNC 2024 Highlights<\/h2>\n

In our fourth year we accomplished a significant expansion in the scope and output of our research community, new research awards, and the inauguration and operation of our Clinical Research Unit.<\/p>\n

Clinical Trials<\/strong>
We are actively investigating 23 rare and ultra-rare brain disorders, with 66 clinical trials underway, and 24 additional trials prepared to launch.
Active Clinical Research Studies ><\/a><\/p>\n

Publications<\/strong>
Publishing multiple basic, clinical and translational research projects focused on neurodevelopmental disorders in 2024
Publications ><\/a><\/p>\n

Events<\/strong>
On September 23, 2024, we hosted over 200 scientists, clinicians, patient advocates, and families in Boston for our fifth full-day symposium entitled \u201cPaving the Path: Clinical Trial Readiness and Developing Therapies for Rare Genetic Disorders\u201d.
RSZ TNC 2024 Symposium ><\/a><\/p>\n

Pilot Grants\u2028Awards of $100,000 each have been made to three new projects.
RSZ TNC Pilot Grants ><\/a><\/p>\n

RSZ TNC Clinical Research Unit<\/strong>
2024 saw the opening at our Two Brookline Place headquarters of state-of-the-art facilities for observational studies and therapeutic clinical trials specific for neurodevelopmental disorders. The new space is dedicated to research on rare and ultra-rare neurogenetic disorders, paving the way for later-stage external investment in new therapeutics.
Clinical Research Unit ><\/a><\/p>\n

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2024 Annual Report<\/h3>\n

[\/et_pb_text][et_pb_image src=”https:\/\/epitomestaging.com\/tnc\/wp-content\/uploads\/2025\/01\/RSZ-AnnualReport-2024.png” alt=”RSZ TNC 2024 Annual Report” title_text=”RSZ-AnnualReport-2024″ url_new_window=”on” align=”center” _builder_version=”4.27.4″ _module_preset=”_initial” background_color=”#ededed” height=”380px” custom_margin=”||-1px|||” custom_padding=”11px|||||” global_colors_info=”{}”][\/et_pb_image][et_pb_text _builder_version=”4.27.4″ _module_preset=”default” background_color=”#ededed” custom_margin=”0px||0px||false|false” custom_padding=”10px|16px|0px|16px|false|true” hover_enabled=”0″ border_style_all=”none” border_color_bottom=”#000000″ border_style_bottom=”none” locked=”off” global_colors_info=”{}” link_text_color__hover_enabled=”on|hover” link_text_color__hover=”#0C71C3″ sticky_enabled=”0″]<\/p>\n

Download the PDF ><\/a><\/p>\n

[\/et_pb_text][\/et_pb_column][\/et_pb_row][\/et_pb_section][et_pb_section fb_built=”1″ _builder_version=”4.16″ _module_preset=”default” background_color=”#ededed” custom_margin=”||||false|false” custom_padding=”24px|0px|29px|0|false|false” global_colors_info=”{}”][et_pb_row column_structure=”2_3,1_3″ use_custom_gutter=”on” gutter_width=”2″ _builder_version=”4.16″ _module_preset=”default” custom_padding=”0px|0px|40px|0px|false|false” global_colors_info=”{}”][et_pb_column type=”2_3″ _builder_version=”4.16″ _module_preset=”default” custom_padding=”|||” global_colors_info=”{}” custom_padding__hover=”|||”][et_pb_text _builder_version=”4.27.4″ _module_preset=”default” custom_margin=”||1px|||” hover_enabled=”0″ global_colors_info=”{}” sticky_enabled=”0″]<\/p>\n

RSZ TNC 2023 Highlights<\/h2>\n

The 2023 report highlights key achievements in our second year of operations including:<\/p>\n

Clinical Trials<\/strong>
Launching a new gene therapy trial for girls with Rett Syndrome in partnership with Neurogene<\/a>
Opening a Clinical Research Unit<\/a> at 2 Brookline Place for clinical trial study visits<\/p>\n

Faculty Members<\/strong>
Recruiting three brilliant new faculty members: Mandana Arbab<\/a>, Jordan Farrell<\/a> and Emily Osterweil<\/a><\/p>\n

Events<\/strong>
Partnering with Global Genes and hosting a panel on the \u201cPower of Partnering\u201d at the Rare Advocacy Summit<\/a> on Collaborative Research for Neurodevelopmental Disorders<\/p>\n

Training Initiatives<\/strong>
Hosting a translational neuroscience fellowship program<\/a>
Awarding 4 RSZ TNC Pilot Grants<\/a>
Launching a new Clinical Psychology Advanced Graduate Practicum<\/a><\/p>\n

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Download the PDF ><\/a><\/p>\n

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RSZ TNC 2022 Highlights<\/h2>\n

<\/strong><\/p>\n

The 2022 report highlights key achievements in our second year of operations including:<\/p>\n

Symposium<\/strong>
Hosting an inaugural symposium entitled Gene Therapy for Pediatric Neurological Disorders and multiple community\/science meetings\u00a0 LEARN MORE ><\/a><\/p>\n

New Advisory Council<\/strong>
Launching a Neuroscience Family Advisory Council research committee to ensure our clinical research includes the patient and family perspective LEARN MORE ><\/a><\/p>\n

Faculty Members<\/strong>
Recruiting two new faculty members to lead RSZ TNC Cores:\u00a0Dr. Jed Hubbs, Director of Medicinal Chemistry Core<\/a> and Dr. Maya Chopra, Director of Translational Genomic Medicine Core<\/a><\/p>\n

Pilot Grants<\/strong>
Awarding two new $100,000 RSZ TNC Pilot grants<\/a><\/p>\n

Human Neuron Core<\/strong>
Sharing of standard operating procedures and tools developed by the Human Neuron Core<\/p>\n

Publications<\/strong>
Publishing a seminal paper proposing a new framework for evaluation of disorders for development of gene therapy, GENE TARGET\u00a0 READ THE PAPER ><\/a><\/p>\n

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Download the PDF ><\/a><\/p>\n

[\/et_pb_text][\/et_pb_column][\/et_pb_row][\/et_pb_section][et_pb_section fb_built=”1″ _builder_version=”4.17.6″ _module_preset=”default” background_color=”#ededed” custom_margin=”50px||||false|false” custom_padding=”24px|0px|29px|0|false|false” locked=”off” global_colors_info=”{}”][et_pb_row column_structure=”2_3,1_3″ use_custom_gutter=”on” gutter_width=”1″ _builder_version=”4.19.4″ _module_preset=”default” background_color=”#ededed” custom_padding=”0px|0px|0|0px|false|false” locked=”off” global_colors_info=”{}”][et_pb_column type=”2_3″ _builder_version=”4.16″ _module_preset=”default” custom_padding=”|||” global_colors_info=”{}” custom_padding__hover=”|||”][et_pb_text _builder_version=”4.27.4″ _module_preset=”default” background_color=”#ededed” custom_margin=”0px||0px||false|false” custom_padding=”10px|16px|0px|16px|false|true” hover_enabled=”0″ global_colors_info=”{}” sticky_enabled=”0″]<\/p>\n

RSZ TNC 2021 Highlights<\/h2>\n

<\/strong><\/p>\n

Leadership Team<\/strong>
Key appointments: Executive Director, new Core Directors, Strategic Advisory Council.<\/p>\n

Fellowship Awards<\/strong>
Two Translational Neuroscience Fellowships<\/a>: the postdoctoral training program is two years in duration.<\/p>\n

Pilot Grants<\/strong>
Four $100,000 awards to principal investigators\u00a0for one-year RSZ TNC Pilot grants<\/a>, with the possibility for a renewal the subsequent year.<\/p>\n

Scientific\/Family Conferences<\/strong>
We partner with patient advocacy groups to plan and conduct meetings between families and researchers. Learn more about\u00a0RSZ TNC Events<\/a>.<\/p>\n

New Gene Therapy Core<\/strong>
Completed national search for two new faculty. Read more about our Core Facilities<\/a>.<\/p>\n

New Clinical and Research Space<\/strong>
The RSZ TNC Research Center at 2 Brookline Place opens in July 2023.<\/p>\n

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“Driving patient-centered research and care forward: A report on the Rosamund Stone Zander Translational Neuroscience Center.”<\/em><\/p>\n

This December 2021 report summarizes the accomplishments achieved in our first year of operations.<\/p>\n

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Download the PDF ><\/a><\/p>\n

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About UsAccomplishmentsRSZ TNC 2024 Highlights In our fourth year we accomplished a significant expansion in the scope and output of our research community, new research awards, and the inauguration and operation of our Clinical Research Unit. Clinical TrialsWe are actively investigating 23 rare and ultra-rare brain disorders, with 66 clinical trials underway, and 24 additional […]<\/p>\n","protected":false},"author":3,"featured_media":0,"parent":0,"menu_order":0,"comment_status":"closed","ping_status":"closed","template":"","meta":{"_acf_changed":false,"_et_pb_use_builder":"on","_et_pb_old_content":"","_et_gb_content_width":"","_monsterinsights_skip_tracking":false,"_monsterinsights_sitenote_active":false,"_monsterinsights_sitenote_note":"","_monsterinsights_sitenote_category":0,"footnotes":""},"class_list":["post-8394","page","type-page","status-publish","hentry"],"acf":[],"_links":{"self":[{"href":"https:\/\/epitomestaging.com\/tnc\/wp-json\/wp\/v2\/pages\/8394","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/epitomestaging.com\/tnc\/wp-json\/wp\/v2\/pages"}],"about":[{"href":"https:\/\/epitomestaging.com\/tnc\/wp-json\/wp\/v2\/types\/page"}],"author":[{"embeddable":true,"href":"https:\/\/epitomestaging.com\/tnc\/wp-json\/wp\/v2\/users\/3"}],"replies":[{"embeddable":true,"href":"https:\/\/epitomestaging.com\/tnc\/wp-json\/wp\/v2\/comments?post=8394"}],"version-history":[{"count":47,"href":"https:\/\/epitomestaging.com\/tnc\/wp-json\/wp\/v2\/pages\/8394\/revisions"}],"predecessor-version":[{"id":12819,"href":"https:\/\/epitomestaging.com\/tnc\/wp-json\/wp\/v2\/pages\/8394\/revisions\/12819"}],"wp:attachment":[{"href":"https:\/\/epitomestaging.com\/tnc\/wp-json\/wp\/v2\/media?parent=8394"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}