For Patients
Partnerships for Muscular Dystrophy
Parent Project Muscular Dystrophy (PPMD)
Parent Project Muscular Dystrophy is committed to ensuring that families affected by Duchenne muscular dystrophy have access to expert healthcare providers, treatments, and a community of support. Their efforts have led to 5 FDA-approved treatments for DMD.
Muscular Dystrophy Association (MDA)
The Muscular Dystrophy Association funds innovative research across the full spectrum of neuromuscular diseases to accelerate development of treatments and cures. The MDA employs a broad reach to facilitate the applicable learnings from one disease to achieve progress in other related diseases.
CLINICAL TRIAL
A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of SRP-9001 in Participants With Duchenne Muscular Dystrophy (DMD) (EMBARK)
PI: Partha Ghosh, MD | Clinical Drug Trial — NCT05096221 >
Patient Advocacy Group Partners: Muscular Dystrophy Association, Parent Project Muscular Dystrophy