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Molly & Robbie
October 13, 2023

7th Annual Cure AP-4 Meeting of Scientific Advisors and Families

The RSZ TNC would like to extend a warm invitation to scientific advisors and families for the 7th annual AP4-Associated HSP Research Conference! This year’s conference includes an ambitious agenda spanning 3 days. Some exciting new developments in the ongoing gene therapy and drug screening projects will be presented, as well as a progress report on the Natural History Study and International Patient Registry. We look forward to productive discussions around next steps for each of these efforts.

The purpose of this meeting is to:

  • Recap what has been learned about AP-4 HSP
  • Discuss progress in the ongoing research projects
  • Discuss human phase 1 trials and gene therapy commercialization

On behalf of the families affected by AP-4-HSP, we truly appreciate your interest in this conference. We are blessed that so many impressive people are involved in the effort to understand and develop treatments for these devastating disorders! For more details, including meeting location and Zoom link information, please download the meeting packet using the link below.

7th Annual Cure AP-4 Meeting Packet (PDF) >

Cure AP-4 Homepage >